CACCIN, PAOLA
CACCIN, PAOLA
The novel use of the CFTR corrector C17 in muscular dystrophy: pharmacological profile and in vivo efficacy
2025 Benetollo, Alberto; Parrasia, Sofia; Scano, Martina; Biasutto, Lucia; Rossa, Andrea; Nogara, Leonardo; Blaauw, Bert; Dalla Barba, Francesco; Caccin, Paola; Carotti, Marcello; Parolin, Alessandro; Akyürek, Eylem Emek; Sacchetto, Roberta; Sandonà, Dorianna
Hydrogel-in-hydrogel live bioprinting for guidance and control of organoids and organotypic cultures
2023 Urciuolo, Anna; Giobbe, Giovanni Giuseppe; Dong, Yixiao; Michielin, Federica; Brandolino, Luca; Magnussen, Michael; Gagliano, Onelia; Selmin, Giulia; Scattolini, Valentina; Raffa, Paolo; Caccin, Paola; Shibuya, Soichi; Scaglioni, Dominic; Wang, Xuechun; Qu, Ju; Nikolic, Marko; Montagner, Marco; Galea, Gabriel L; Clevers, Hans; Giomo, Monica; De Coppi, Paolo; Elvassore, Nicola
C17 corrector for the treatment of sarcoglycanopathy: preliminary ADME studies
2022 Benetollo, Alberto; Scano, Martina; Parrasia, Sofia; Biasutto, Lucia; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sandona', Dorianna
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
2022 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondì, Michela; DALLA BARBA, Francesco; Soardi, Michela; Furlan, Sandra; Akyurek, EYLEM EMEK; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandonà, Dorianna
Customized bioreactor enables the production of 3D diaphragmatic constructs influencing matrix remodeling and fibroblast overgrowth
2022 Maghin, E.; Carraro, E.; Boso, D.; Dedja, A.; Giagante, M.; Caccin, P.; Barna, R. A. -M.; Bresolin, S.; Cani, A.; Borile, G.; Sandrin, D.; Romanato, F.; Cecchinato, F.; Urciuolo, A.; Sandona, D.; De Coppi, P.; Pavan, P. G.; Piccoli, M.
Nerve-dependent distribution of subsynaptic type 1 inositol 1,4,5-trisphosphate receptor at the neuromuscular junction
2022 Volpe, Pompeo; Bosutti, Alessandra; Nori, Alessandra; Filadi, Riccardo; Gherardi, Gaia; Trautmann, Gabor; Furlan, Sandra; Massaria, Gabriele; Sciancalepore, Marina; Megighian, Aram; Caccin, Paola; Bernareggi, Annalisa; Salanova, Michele; Sacchetto, Roberta; Sandona, Dorianna; Pizzo, Paola; Lorenzon, Paola
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype
2022 DALLA BARBA, Francesco; Soardi, Michela; Scano, Martina; Benetollo, Alberto; Carotti, Marcello; Caccin, Paola; Risato, Giovanni; Argenton, Francesco; Sandonà, Dorianna
Decellularized skeletal muscles support the generation of in vitro neuromuscular tissue models
2021 Raffa, P.; Easler, M.; Cecchinato, F.; Auletta, B.; Scattolini, V.; Perin, S.; Gerli, M. F. M.; Caccin, P.; Elvassore, N.; De Coppi, P.; Urciuolo, A.
In vivo proof of concept of the efficacy of the CFTR corrector C17 in a sarcoglycanopathy mouse model
2021 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondi', Michela; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo rescue of α-sarcoglycan mutants by CFTR correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
Decellularized skeletal muscles display neurotrophic effects in three-dimensional organotypic cultures
2020 Raffa, P.; Scattolini, V.; Gerli, M. F. M.; Perin, S.; Cui, M.; De Coppi, P.; Elvassore, N.; Caccin, P.; Luni, C.; Urciuolo, A.
A novel bioreactor to improve myogenic cell alignement and maturation into a functional diaphragm-like muscle tissue
2019 Maghin, E.; Carraro, E.; Boso, D.; de Cesare, N.; Giagante, M.; Caccin, P.; Gamba, P.; De Coppi, P.; Pavan, P.; Piccoli, M.
Allogenic tissue-specific decellularized scaffolds promote long-term muscle innervation and functional recovery in a surgical diaphragmatic hernia model
2019 Trevisan, Caterina; Maghin, Edoardo; Dedja, Arben; Caccin, Paola; de Cesare, Niccolò; Franzin, Chiara; Boso, Daniele; Pesce, Paola; Caicci, Federico; Boldrin, Francesco; Urbani, Luca; De Coppi, Paolo; Pozzobon, Michela; Pavan, Piero; Piccoli, Martina
Generation of a Functioning and Self-Renewing Diaphragmatic Muscle Construct
2019 Trevisan, Caterina; Fallas, Mario Enrique Alvrez; Maghin, Edoardo; Franzin, Chiara; Pavan, Piero; Caccin, Paola; Chiavegato, Angela; Carraro, Eugenia; Boso, Daniele; Boldrin, Francesco; Caicci, Federico; Bertin, Enrica; Urbani, Luca; Milan, Anna; Biz, Carlo; Lazzari, Lorenza; De Coppi, Paolo; Pozzobon, Michela; Piccoli, Martina
Diaphragmatic-derived extracellular matrix patch exerts a positive long lasting effect on myogenic regeneration and nerve attraction when used in a surgical mouse model of diaphragmatic hernia
2018 Trevisan, Caterina; Dedja, Arben; Maghin, Edoardo; Pavan, Piero; Caccin, Paola; Franzin, Chiara; DE CESARE, Niccolo'; Urbani, Luca; DE COPPI, Paolo; Pozzobon, Michela; Piccoli, Martina
Mouse Phrenic Nerve Hemidiaphragm Assay (MPN)
2018 Zanetti, Giulia; Negro, Samuele; Pirazzini, Marco; Caccin, Paola
The synaptotagmin juxtamembrane domain is involved in neuroexocytosis
2015 Caccin, Paola; Scorzeto, Michele; Damiano, Nunzio; Marin, Oriano; Megighian, Aram; Montecucco, Cesare
Nidogens are therapeutic targets for the prevention of tetanus
2014 K., Bercsenyi; N., Schmieg; J. B., Bryson; M., Wallace; Caccin, Paola; M., Golding; Zanotti, Giuseppe; L., Greensmith; R., Nischt; G., Schiavo