SANDONA', DORIANNA
SANDONA', DORIANNA
Dipartimento di Scienze Biomediche - DSB
The novel use of the CFTR corrector C17 in muscular dystrophy: pharmacological profile and in vivo efficacy
2025 Benetollo, Alberto; Parrasia, Sofia; Scano, Martina; Biasutto, Lucia; Rossa, Andrea; Nogara, Leonardo; Blaauw, Bert; Dalla Barba, Francesco; Caccin, Paola; Carotti, Marcello; Parolin, Alessandro; Akyürek, Eylem Emek; Sacchetto, Roberta; Sandonà, Dorianna
Advanced therapeutic approaches in sarcoglycanopathies
2024 Scano, M.; Benetollo, A.; Dalla Barba, F.; Sandona, D.
Brody Disease: Utilizing a Novel Zebrafish Animal Model for Exploring Potential Therapeutic Strategies for this Rare Human Condition
2024 Akyurek, EYLEM EMEK; DALLA BARBA, Francesco; Carotti, Marcello; Greco, Francesca; Gorni, Giulia; Fonsatti, Elisa; Vettori, Andrea; Sandonà, Dorianna; Sacchetto, Roberta
Efficacy of Cystic Fibrosis Transmembrane Regulator Corrector C17 in Beta-Sarcoglycanopathy—Assessment of Patient’s Primary Myotubes
2024 Scano, Martina; Benetollo, Alberto; Dalla Barba, Francesco; Akyurek, Eylem Emek; Carotti, Marcello; Sacchetto, Roberta; Sandonà, Dorianna
Fetal bovine serum contains biologically available ATP
2024 Vultaggio-Poma, Valentina; Scussel Bergamin, Leticia; Falzoni, Simonetta; Tarantini, Mario; Giuliani, Anna Lisa; Sandonà, Dorianna; Polverino De Laureto, Patrizia; Di Virgilio, Francesco
The Accordion Zebrafish tq206 Mutant in the Assessment of a Novel Pharmaceutical Approach to Brody Myopathy
2024 Akyurek, EYLEM EMEK; Greco, Francesca; Tesoriero, Chiara; DALLA BARBA, Francesco; Carotti, Marcello; Gorni, Giulia; Sandonà, Dorianna; Vettori, Andrea; Sacchetto, Roberta
Brody Disease: A Novel Zebrafish Animal Model to Test Potential Therapeutic Approach for This Rare Human Disease
2023 Akyurek, EYLEM EMEK; DALLA BARBA, Francesco; Carotti, Marcello; Greco, Francesca; Gorni, Giulia; Fonsatti, Elisa; Vettori, Andrea; Sandona, Dorianna; Sacchetto, Roberta
CATTLE CONGENITAL PSEUDOMYOTONIA AS ANIMAL MODEL: WHEN DIAPHRAGM MUSCLE CAN MAKE THE DIFFERENCE
2023 Akyurek, EYLEM EMEK; Jacinto, JOANA G. P.; Bolcato, Marilena; Bianchini, Elisa; Sandonà, Dorianna; Gentile, Arcangelo; Sacchetto, Roberta
Modeling Sarcoglycanopathy in Danio rerio
2023 Dalla Barba, Francesco; Soardi, Michela; Mouhib, Leila; Risato, Giovanni; Akyürek, Eylem Emek; Lucon-Xiccato, Tyrone; Scano, Martina; Benetollo, Alberto; Sacchetto, Roberta; Richard, Isabelle; Argenton, Francesco; Bertolucci, Cristiano; Carotti, Marcello; Sandonà, Dorianna
Synthesis and Evaluation of Bithiazole Derivatives As Potential α-Sarcoglycan Correctors
2023 Ribaudo, Giovanni; Carotti, Marcello; Ongaro, Alberto; Oselladore, Erika; Scano, Martina; Zagotto, Giuseppe; Sandonà, Dorianna; Gianoncelli, Alessandra
Brody Disease: A Novel Potential Therapeutic Approach for This Rare Human Disease
2022 Akyurek, EYLEM EMEK; Jacinto, JOANA GP; Bolcato, Marilena; Bianchini, Elisa; Sandonà, Dorianna; Gentile, Arcangelo; Sacchetto, Roberta.
C17 corrector for the treatment of sarcoglycanopathy: preliminary ADME studies
2022 Benetollo, Alberto; Scano, Martina; Parrasia, Sofia; Biasutto, Lucia; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sandona', Dorianna
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
2022 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondì, Michela; DALLA BARBA, Francesco; Soardi, Michela; Furlan, Sandra; Akyurek, EYLEM EMEK; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandonà, Dorianna
Customized bioreactor enables the production of 3D diaphragmatic constructs influencing matrix remodeling and fibroblast overgrowth
2022 Maghin, E.; Carraro, E.; Boso, D.; Dedja, A.; Giagante, M.; Caccin, P.; Barna, R. A. -M.; Bresolin, S.; Cani, A.; Borile, G.; Sandrin, D.; Romanato, F.; Cecchinato, F.; Urciuolo, A.; Sandona, D.; De Coppi, P.; Pavan, P. G.; Piccoli, M.
Differential Analysis of Gly211Val and Gly286Val Mutations Affecting Sarco(endo)plasmic Reticulum Ca2+-ATPase (SERCA1) in Congenital Pseudomyotonia Romagnola Cattle
2022 Akyurek, Eylem Emek; Busato, Francesca; Murgiano, Leonardo; Bianchini, Elisa; Carotti, Marcello; Sandonà, Dorianna; Drögemüller, Cord; Gentile, Arcangelo; Sacchetto, Roberta
Dystrophic Muscle Affects Motoneuron Axon Outgrowth and NMJ Assembly
2022 Fornetti, E.; Testa, S.; De Paolis, F.; Fuoco, C.; Bernardini, S.; Pozo Devoto, V.; Stokin, G. B.; Giannitelli, S. M.; Rainer, A.; Bigot, A.; Zoccali, C.; Baldi, J.; Sandona, D.; Rizzi, R.; Bearzi, C.; Forte, G.; Cannata, S.; Gargioli, C.
Human Brody disease and novel therapeutic approaches of its animal model cattle pseudomyotonia
2022 Akyurek, EYLEM EMEK; Jacinto, JOANA GP; Bolcato, Marilena; Bianchini, Elisa; Sandonà, Dorianna; Gentile, Arcangelo; Sacchetto, Roberta.
Nerve-dependent distribution of subsynaptic type 1 inositol 1,4,5-trisphosphate receptor at the neuromuscular junction
2022 Volpe, Pompeo; Bosutti, Alessandra; Nori, Alessandra; Filadi, Riccardo; Gherardi, Gaia; Trautmann, Gabor; Furlan, Sandra; Massaria, Gabriele; Sciancalepore, Marina; Megighian, Aram; Caccin, Paola; Bernareggi, Annalisa; Salanova, Michele; Sacchetto, Roberta; Sandona, Dorianna; Pizzo, Paola; Lorenzon, Paola
Targeting of PFKFB3 with miR-206 but not mir-26b inhibits ovarian cancer cell proliferation and migration involving FAK downregulation
2022 Boscaro, Carlotta; Baggio, Chiara; Carotti, Marcello; Sandonà, Dorianna; Trevisi, Lucia; Cignarella, Andrea; Bolego, Chiara
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype
2022 DALLA BARBA, Francesco; Soardi, Michela; Scano, Martina; Benetollo, Alberto; Carotti, Marcello; Caccin, Paola; Risato, Giovanni; Argenton, Francesco; Sandonà, Dorianna