CAROTTI, MARCELLO
CAROTTI, MARCELLO
CFTR corrector C17 rescues defective SERCA1 in bovine pseudomyotonia: a potential therapy for Brody myopathy
2025 Akyürek, Eylem E; Jacinto, Joana Gonçalves Pontes; Iori, Silvia; Bianchini, Elisa; Bolcato, Marilena; Costa, Roberta; Giantin, Mery; Carotti, Marcello; Dacasto, Mauro; Cenacchi, Giovanna; Sandonà, Dorianna; Gentile, Arcangelo; Sacchetto, Roberta
Nanohybridization as a Route to a Water-Friendly Therapeutic Tool for Rescuing Misfolded Proteins
2025 Bortoluzzi, Mary; Cencini, Aura; Rutigliano, Lavinia; Rilievo, Graziano; Cecconello, Alessandro; Tonolo, Federica; Molinari, Simone; Sacchetto, Roberta; Carotti, Marcello; Sandonà, Dorianna; Martinello, Tiziana; Ugolotti, Juri; Fresch, Barbara; Litti, Lucio; Vianello, Fabio; Magro, Massimiliano
The novel use of the CFTR corrector C17 in muscular dystrophy: pharmacological profile and in vivo efficacy
2025 Benetollo, Alberto; Parrasia, Sofia; Scano, Martina; Biasutto, Lucia; Rossa, Andrea; Nogara, Leonardo; Blaauw, Bert; Dalla Barba, Francesco; Caccin, Paola; Carotti, Marcello; Parolin, Alessandro; Akyürek, Eylem Emek; Sacchetto, Roberta; Sandonà, Dorianna
Brody Disease: Utilizing a Novel Zebrafish Animal Model for Exploring Potential Therapeutic Strategies for this Rare Human Condition
2024 Akyurek, EYLEM EMEK; DALLA BARBA, Francesco; Carotti, Marcello; Greco, Francesca; Gorni, Giulia; Fonsatti, Elisa; Vettori, Andrea; Sandonà, Dorianna; Sacchetto, Roberta
Efficacy of Cystic Fibrosis Transmembrane Regulator Corrector C17 in Beta-Sarcoglycanopathy—Assessment of Patient’s Primary Myotubes
2024 Scano, Martina; Benetollo, Alberto; Dalla Barba, Francesco; Akyurek, Eylem Emek; Carotti, Marcello; Sacchetto, Roberta; Sandonà, Dorianna
The Accordion Zebrafish tq206 Mutant in the Assessment of a Novel Pharmaceutical Approach to Brody Myopathy
2024 Akyurek, EYLEM EMEK; Greco, Francesca; Tesoriero, Chiara; DALLA BARBA, Francesco; Carotti, Marcello; Gorni, Giulia; Sandonà, Dorianna; Vettori, Andrea; Sacchetto, Roberta
Brody Disease: A Novel Zebrafish Animal Model to Test Potential Therapeutic Approach for This Rare Human Disease
2023 Akyurek, EYLEM EMEK; DALLA BARBA, Francesco; Carotti, Marcello; Greco, Francesca; Gorni, Giulia; Fonsatti, Elisa; Vettori, Andrea; Sandona, Dorianna; Sacchetto, Roberta
Exploiting HOPNO-dicopper center interaction to development of inhibitors for human tyrosinase
2023 Buitrago, E.; Faure, C.; Carotti, M.; Bergantino, E.; Hardre, R.; Maresca, M.; Philouze, C.; Vanthuyne, N.; Boumendjel, A.; Bubacco, L.; du Moulinet d'Hardemare, A.; Jamet, H.; Reglier, M.; Belle, C.
Modeling Sarcoglycanopathy in Danio rerio
2023 Dalla Barba, Francesco; Soardi, Michela; Mouhib, Leila; Risato, Giovanni; Akyürek, Eylem Emek; Lucon-Xiccato, Tyrone; Scano, Martina; Benetollo, Alberto; Sacchetto, Roberta; Richard, Isabelle; Argenton, Francesco; Bertolucci, Cristiano; Carotti, Marcello; Sandonà, Dorianna
Synthesis and Evaluation of Bithiazole Derivatives As Potential α-Sarcoglycan Correctors
2023 Ribaudo, Giovanni; Carotti, Marcello; Ongaro, Alberto; Oselladore, Erika; Scano, Martina; Zagotto, Giuseppe; Sandonà, Dorianna; Gianoncelli, Alessandra
C17 corrector for the treatment of sarcoglycanopathy: preliminary ADME studies
2022 Benetollo, Alberto; Scano, Martina; Parrasia, Sofia; Biasutto, Lucia; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sandona', Dorianna
CFTR corrector C17 is effective in muscular dystrophy, in vivo proof of concept in LGMDR3
2022 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondì, Michela; DALLA BARBA, Francesco; Soardi, Michela; Furlan, Sandra; Akyurek, EYLEM EMEK; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandonà, Dorianna
Differential Analysis of Gly211Val and Gly286Val Mutations Affecting Sarco(endo)plasmic Reticulum Ca2+-ATPase (SERCA1) in Congenital Pseudomyotonia Romagnola Cattle
2022 Akyurek, Eylem Emek; Busato, Francesca; Murgiano, Leonardo; Bianchini, Elisa; Carotti, Marcello; Sandonà, Dorianna; Drögemüller, Cord; Gentile, Arcangelo; Sacchetto, Roberta
Targeting of PFKFB3 with miR-206 but not mir-26b inhibits ovarian cancer cell proliferation and migration involving FAK downregulation
2022 Boscaro, Carlotta; Baggio, Chiara; Carotti, Marcello; Sandonà, Dorianna; Trevisi, Lucia; Cignarella, Andrea; Bolego, Chiara
Zebrafish as a model for sarcoglycanopathies: in-depth analysis of the disease phenotype
2022 DALLA BARBA, Francesco; Soardi, Michela; Scano, Martina; Benetollo, Alberto; Carotti, Marcello; Caccin, Paola; Risato, Giovanni; Argenton, Francesco; Sandonà, Dorianna
Ditopic Chelators of Dicopper Centers for Enhanced Tyrosinases Inhibition
2021 Buitrago, E.; Faure, C.; Challali, L.; Bergantino, E.; Boumendjel, A.; Bubacco, L.; Carotti, M.; Hardre, R.; Maresca, M.; Philouze, C.; Jamet, H.; Reglier, M.; Belle, C.
In vivo proof of concept of the efficacy of the CFTR corrector C17 in a sarcoglycanopathy mouse model
2021 Scano, Martina; Benetollo, Alberto; Nogara, Leonardo; Bondi', Michela; DALLA BARBA, Francesco; Caccin, Paola; Carotti, Marcello; Sacchetto, Roberta; Blaauw, Bert; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo recovery of α-sarcoglycan mutants by protein folding correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna
In vivo rescue of α-sarcoglycan mutants by CFTR correctors
2021 Scano, Martina; Benetollo, Alberto; Bondi', Michela; Caccin, Paola; Carotti, Marcello; DALLA BARBA, Francesco; Soardi, Michela; Sacchetto, Roberta; Sandona', Dorianna