COLOMBATTI, RAFFAELLA
COLOMBATTI, RAFFAELLA
Dipartimento di Salute della Donna e del Bambino - SDB
Safety and efficacy of mitapivat in sickle cell disease (RISE UP): results from the phase 2 portion of a global, double-blind, randomised, placebo-controlled trial
2025 Idowu, Modupe; Otieno, Lucas; Dumitriu, Bogdan; Lobo, Clarisse L C; Thein, Swee Lay; Andemariam, Biree; Nnodu, Obiageli E; Inati, Adlette; Glaros, Alexander K; Bartolucci, Pablo; Colombatti, Raffaella; Taher, Ali T; Abboud, Miguel R; Darbari, Deepika; Ataga, Kenneth I; Antmen, Ali Bülent; Kuo, Kevin H M; de Souza Medina, Samuel; Oluyadi, Abdulafeez; Iyer, Varsha; Morris, Susan; Yates, Amber M; Shao, Hui; Patil, Spurthi; Urbstonaitis, Rolandas; Zaidi, Ahmar U; Gheuens, Sarah; Smith, Wally R
Are we ready for new strategies to prevent stroke in children with sickle cell disease?
2024 Russo, Giovanna; Colombatti, Raffaella
Early-onset indicators of a hypercoagulable state and clinical complications in a cohort of children with sickle cell trait
2024 Reggiani, Giulia; Boaro, Maria Paola; Menzato, Federica; De Bon, Emiliano; Bertomoro, Antonella; Casonato, Alessandra; Lucente, Fabrizio; Fortino, Cecilia; Sartori, Mariateresa; Steffan, Agostino; Martella, Maddalena; D'Agnolo, Mirco; Sainati, Laura; Colombatti, Raffaella
Limited access to transcranial Doppler screening and stroke prevention for children with sickle cell disease in Europe: Results of a multinational EuroBloodNet survey
2024 Voi, Vincenzo; Gutierrez-Valle, Victoria; Cuzzubbo, Daniela; Mcmahon, Corrina; Casale, Maddalena; Mañú Pereira, Maria Del Mar; D'Agnolo, Mirco; Inusa, Baba P D; de Montalembert, Mariane; Colombatti, Raffaella
Posterior cerebral circulation in children with sickle cell anemia: an uncharted territory
2024 Salimbeni, Alvise Fattorello; De Rosa, Ludovica; Volpato, Alessia; Viaro, Federica; Pieroni, Alessio; Mozzetta, Stefano; Favruzzo, Francesco; Pes, Alessandra; Zaccagnino, Matteo; Reggiani, Giulia; Boaro, Maria Paola; Colombatti, Raffaella; Manara, Renzo; Baracchini, Claudio
Real‐World Evidence of Crizanlizumab Showing Reductions in Vaso‐Occlusive Crises and Opioid Usage in Sickle Cell Disease
2024 Debonnett, Laurie; Joshi, Vikas; Silva‐pinto, Ana Cristina; Colombatti, Raffaella; Pasanisi, Annamaria; Arcioni, Francesco; Cançado, Rodolfo D.; Sarp, Séverine; Sarkar, Rajendra; Soliman, Wesam
Structural and functional characterization of an individual with the M285R KCNV2 hypomorphic allele
2024 de Guimaraes, Thales A. C.; Lai, Francesco; Colombatti, Raffaella; Sato, Giovanni; Rizzo, Roberta; Kalitzeos, Angelos; Michaelides, Michel
Acute chest syndrome in children with sickle cell disease: Data from a national AIEOP cohort identify priority areas of intervention in a hub-and-spoke system
2023 Munaretto, V; Corti, P; Bertoni, E; Tripodi, S I; Guerzoni, M E; Cesaro, S; Arcioni, F; Piccolo, C; Mina, T; Zecca, M; Cuzzubbo, D; Casale, M; Palazzi, G; Notarangelo, L D; Masera, N; Samperi, P; Perrotta, S; Russo, G; Sainati, L; Colombatti, R
Challenges and Opportunities of Precision Medicine in Sickle Cell Disease: Novel European Approach by GenoMed4All Consortium and ERN-EuroBloodNet
2023 Collado, Anna; Boaro, Maria Paola; van der Veen, Sigrid; Idrizovic, Amira; Biemond, Bart J; Beneitez Pastor, David; Ortuño, Ana; Cela, Elena; Ruiz-Llobet, Anna; Bartolucci, Pablo; de Montalembert, Marianne; Castellani, Gastone; Biondi, Riccardo; Manara, Renzo; Sanavia, Tiziana; Fariselli, Piero; Kountouris, Petros; Kleanthous, Marina; Alvarez, Federico; Zazo, Santiago; Colombatti, Raffaella; van Beers, Eduard J; Mañú-Pereira, María Del Mar
CK2β Regulates Hematopoietic Stem Cell Biology and Erythropoiesis
2023 Quotti Tubi, L.; Canovas Nunes, S.; Mandato, E.; Pizzi, M.; Vitulo, N.; D'Agnolo, M.; Colombatti, R.; Martella, M.; Boaro, M. P.; Doriguzzi Breatta, E.; Fregnani, A.; Spinello, Z.; Nabergoj, M.; Filhol, O.; Boldyreff, B.; Albiero, M.; Fadini, G. P.; Gurrieri, C.; Vianello, F.; Semenzato, G.; Manni, S.; Trentin, L.; Piazza, F.
Defining global strategies to improve outcomes in sickle cell disease: a Lancet Haematology Commission
2023 Piel, Frédéric B; Rees, David C; Debaun, Michael R; Nnodu, Obiageli; Ranque, Brigitte; Thompson, Alexis A; Ware, Russell E; Abboud, Miguel R; Abraham, Allistair; Ambrose, Emmanuela E; Andemariam, Biree; Colah, Roshan; Colombatti, Raffaella; Conran, Nicola; Costa, Fernando F; Cronin, Robert M; de Montalembert, Mariane; Elion, Jacques; Esrick, Erica; Greenway, Anthea L; Idris, Ibrahim M; Issom, David-Zacharie; Jain, Dipty; Jordan, Lori C; Kaplan, Zane S; King, Allison A; Lloyd-Puryear, Michele; Oppong, Samuel A; Sharma, Akshay; Sung, Lillian; Tshilolo, Leon; Wilkie, Diana J; Ohene-Frempong, Kwaku
Early splenectomy in sickle cell disease: another piece of the puzzle
2023 Colombatti, Raffaella; Casale, Maddalena
Haemochromatosis in children: A national retrospective cohort promoted by the A.I.E.O.P. (Associazione Italiana Emato‐Oncologia Pediatrica) study group
2023 Corti, Paola; Ferrari, Giulia Maria; Faraguna, Martha Caterina; Capitoli, Giulia; Longo, Filomena; Corradini, Elena; Casini, Tommaso; Boscarol, Gianluca; Pinto, Valeria Maria; Ghilardi, Roberta; Russo, Giovanna; Colombatti, Raffaella; Mariani, Raffaella; Piperno, Alberto
Hematological characteristics and hepatobiliary complications of hereditary spherocytosis in a tertiary care pediatric center: optimizing diagnosis and care through local and international networks
2023 Boaro, Maria Paola; Reggiani, Giulia; D’Agnolo, Mirco; Munaretto, Vania; Pozzebon, Francesco; Trapanese, Roberta; Martella, Maddalena; Colombatti, Raffaella
Pain Frequency and Health Care Utilization Patterns in Women with Sickle Cell Disease Experiencing Menstruation-Associated Pain Crises
2023 Segbefia, Catherine; Campbell, Jillian; Tartaglione, Immacolata; Asare, Eugenia Vicky; Andemariam, Biree; Zempsky, William; Colombatti, Raffaella; Boatemaa, Gifty Dankwah; Boruchov, Donna; Rao, Sudha; Piccone, Connie M.; Smith, Ashya; Haile, Haikel; Kim, Esther; Wilson, Samuel; Farooq, Fatimah; Urbonya, Rebekah; Rivers, Angela; Manwani, Deepa; Gai, Jiaxiang; Sey, Fredericka; Inusa, Baba; Antwi-Boasiako, Charles; Strunk, Crawford; Campbell, Andrew D.
Prevention of neurovascular complications in children with Sickle Cell Disease in the real-world setting: What adult medicine physicians should know
2023 Reggiani, Giulia; Boaro, Maria Paola; Colombatti, Raffaella
Relationship between hemoglobin, hemolysis, and transcranial Doppler velocities in children with sickle cell disease: Results from a long-term natural history study in Italy in the era of multimodal therapy
2023 Reggiani, Giulia; Coppadoro, Beatrice; Munaretto, Vania; Pieroni, Alessio; Viaro, Federica; Manara, Renzo; Beaubrun, Anne; Biffi, Alessandra; Baracchini, Claudio; Sainati, Laura; Colombatti, Raffaella
Severe hemolytic anemia in a newborn: Look out for rare Gardos channelopathies due to KCNN4 mutation
2023 Munaretto, Vania; Martella, Maddalena; Francescato, Samuela; Reggiani, Giulia; Boaro, Maria Paola; Bianchi, Paola; Fermo, Elisa; Barcellini, Wilma; Sainati, Laura; Colombatti, Raffaella
Sickle cell disease landscape and challenges in the EU: the ERN-EuroBloodNet perspective
2023 Mañú Pereira, María Del Mar; Colombatti, Raffaella; Alvarez, Federico; Bartolucci, Pablo; Bento, Celeste; Brunetta, Angelo Loris; Cela, Elena; Christou, Soteroula; Collado, Anna; de Montalembert, Mariane; Dedeken, Laurence; Fenaux, Pierre; Galacteros, Frédéric; Glenthøj, Andreas; Gutiérrez Valle, Victoria; Kattamis, Antonis; Kunz, Joachim; Lobitz, Stephan; Mcmahon, Corrina; Pellegrini, Mariangela; Reidel, Sara; Russo, Giovanna; Santos Freire, Miriam; van Beers, Eduard; Kountouris, Petros; Gulbis, Béatrice
Sickle cell disease: embedding patient participation into an international conference can transform the role of lived experience
2023 Pellegrini, Mariangela; Chakravorty, Subarna; del Mar Manu Pereira, Maria; Gulbis, Beatrice; Gilmour-Hamilton, Catriona; Hayes, Sandy; de Montalembert, Mariane; Inusa, Baba Psalm Duniya; Colombatti, Raffaella; Roy, Noémi BA